Αποτελέσματα Αναζήτησης
8 Νοε 2023 · In this article, we highlight success and ongoing challenges in three areas of high activity in gene therapy: inherited blood cell diseases by targeting hematopoietic stem cells, malignant...
- Gene therapy and gene correction: targets, progress, and challenges for ...
Full size table. Disease targets and strategies for gene...
- Gene therapy and gene correction: targets, progress, and challenges for ...
1 Δεκ 2018 · This review focuses on the application of gene therapy for the correction of inherited diseases, the limitations and drawbacks encountered in some of the early clinical trials and the revival...
1 Ιαν 2019 · PDF | On Jan 1, 2019, Susanne Hempel published Gene Therapy in 2019: Milestones and Challenges | Find, read and cite all the research you need on ResearchGate.
8 Νοε 2023 · In this article, we highlight success and ongoing challenges in three areas of high activity in gene therapy: inherited blood cell diseases by targeting hematopoietic stem cells, malignant...
7 Μαΐ 2024 · To address this knowledge gap, this review summarizes core principles, benefits, potential risks and challenges of gene therapy, with a particular focus on hemophilia and spinal muscular atrophy, and discusses future perspectives.
27 Ιαν 2024 · Download Full Issue. Current challenges in cell and gene therapy: a joint view from the European Committee of the International Society for Cell & Gene Therapy (ISCT) and the European Society for Blood and Marrow Transplantation (EBMT)
9 Οκτ 2020 · Full size table. Disease targets and strategies for gene therapy. Gene therapy techniques are aimed at treating a variety of human diseases, including dominant and recessive genetic...