Αποτελέσματα Αναζήτησης
8 Νοε 2023 · In this article, we highlight success and ongoing challenges in three areas of high activity in gene therapy: inherited blood cell diseases by targeting hematopoietic stem cells, malignant...
- Gene therapy and gene correction: targets, progress, and challenges for ...
Gene therapy and gene correction techniques have developed...
- Gene therapy and gene correction: targets, progress, and challenges for ...
9 Οκτ 2020 · Gene therapy and gene correction techniques have developed rapidly over the last several decades, aimed at treating genetic diseases for which current treatment options are limited or...
7 Μαΐ 2024 · To address this knowledge gap, this review summarizes core principles, benefits, potential risks and challenges of gene therapy, with a particular focus on hemophilia and spinal muscular atrophy, and discusses future perspectives.
24 Αυγ 2022 · This review discusses in detail the current challenges surrounding the practice of gene therapy, focusing on the moral arguments and scientific claims that affect the advancement of the technology. The review also suggests precautionary principles as a means to navigate ethical uncertainties.
1 Ιουν 2022 · Here we compare current gene therapy development efforts with major health priorities in under-resourced areas. We then contrast gene therapy needs with access to gene therapy clinical trials and licensed products.
8 Σεπ 2024 · This achievement marked a historic moment as Glybera became the first gene therapy treatment to be authorized in Europe, setting a precedent for future gene-based therapies. 19 Nonetheless, despite its groundbreaking status, Glybera® faced challenges related to its cost-effectiveness. With a staggering price tag exceeding €1 million per ...
8 Νοε 2023 · In this article, we highlight success and ongoing challenges in three areas of high activity in gene therapy: inherited blood cell diseases by targeting hematopoietic stem cells, malignant disorders using immune effector cells genetically modified with chimeric antigen receptors, and ophthalmologic, neurologic, and coagulation disorders using ...
