Αποτελέσματα Αναζήτησης
1 Δεκ 2018 · This review focuses on the application of gene therapy for the correction of inherited diseases, the limitations and drawbacks encountered in some of the early clinical trials and the revival...
8 Νοε 2023 · In this article, we highlight success and ongoing challenges in three areas of high activity in gene therapy: inherited blood cell diseases by targeting hematopoietic stem cells, malignant...
7 Μαΐ 2024 · The purpose of this review is to provide an overview of the core principles of gene therapy along with information on challenges and risks. Benefits, adverse effects and potential risks are illustrated based on the examples of hemophilia and spinal muscular atrophy.
1 Σεπ 2017 · Gene therapy is proven to be a potential disease-modifying treatment for AD. This article discusses about gene therapy, its merits and demerits and the various ways of gene delivery.
Challenges to gene therapy. One of the most important issues regarding gene therapy is safety. Gene therapy research took a step backward in 1999 following the death of Jesse...
1 Νοε 2023 · A comprehensive review of the current clinical trials involving gene therapy for AD and PD discusses the challenges and opportunities associated with the gene therapy approach and ongoing developments related to increasing the safety and efficacy of the gene therapy for long-term outcomes.
9 Οκτ 2020 · Gene correction using CRISPR-Cas9 is an extension of gene therapy that has received considerable attention in recent years and boasts many possible uses beyond classical gene therapy...
