Αποτελέσματα Αναζήτησης
8 Νοε 2023 · In this article, we highlight success and ongoing challenges in three areas of high activity in gene therapy: inherited blood cell diseases by targeting hematopoietic stem cells, malignant...
- Gene therapy and gene correction: targets, progress, and challenges for ...
Gene therapy and gene correction techniques have developed...
- Gene therapy and gene correction: targets, progress, and challenges for ...
In this review, we summarize the key advancements in gene therapy for ED treatment, with an emphasis on the emerging stem cell-based approaches as well as other combinational strategies. The challenges facing the clinical application of gene therapy for ED treatment are also discussed.
8 Σεπ 2024 · This achievement marked a historic moment as Glybera became the first gene therapy treatment to be authorized in Europe, setting a precedent for future gene-based therapies. 19 Nonetheless, despite its groundbreaking status, Glybera® faced challenges related to its cost-effectiveness. With a staggering price tag exceeding €1 million per ...
9 Οκτ 2020 · Gene therapy and gene correction techniques have developed rapidly over the last several decades, aimed at treating genetic diseases for which current treatment options are limited or...
7 Μαΐ 2024 · To address this knowledge gap, this review summarizes core principles, benefits, potential risks and challenges of gene therapy, with a particular focus on hemophilia and spinal muscular atrophy, and discusses future perspectives.
12 Φεβ 2020 · The scientific, technical and ethical aspects of using CRISPR technology for therapeutic applications in humans are discussed, highlighting both opportunities and challenges of this technology...
The ability to make site-specific modifications to the human genome has been an objective in medicine since the recognition of the gene as the basic unit of heredity. Thus, gene therapy is understood as the ability of genetic improvement through the correction of altered (mutated) genes or site-spec ….
