Αποτελέσματα Αναζήτησης
16 Μαΐ 2019 · Gene therapy encompasses multiple approaches to manipulate genetic material in an effort to treat specific diseases, including replacing a mutated or defective gene with a healthy one, introducing a new gene to help fight disease, or editing an existing gene to change its function [1].
7 Ιουλ 2021 · Preclinical research suggested that the investigational gene therapy (GT; used without intending to imply a therapeutic effect) might slow or halt disease progression—a unique prospect for...
8 Νοε 2023 · In this article, we highlight success and ongoing challenges in three areas of high activity in gene therapy: inherited blood cell diseases by targeting hematopoietic stem cells, malignant...
23 Απρ 2024 · Gene therapy aims to fix a faulty gene or replace it with a healthy gene to try to cure disease or make the body better able to fight disease. It holds promise as a treatment for a wide range of diseases, such as cancer, cystic fibrosis, heart disease, diabetes, hemophilia and AIDS.
25 Μαΐ 2021 · Gene therapy restored immune system function to children with an inherited immune disorder with fewer side effects than existing therapies. The therapy could be a safe and effective treatment for this rare and life-threatening condition.
6 Ιουν 2014 · There are a wide variety of potential gene and cell therapies in various stages of development. Patients who received first gene therapy treatments for primary immune deficiencies (PIDs) are reaching 10 and 15 years post-treatment, with robust and sustained immune recovery.
24 Ιαν 2024 · A novel gene therapy approach has given five children who were born deaf the ability to hear. The method, which overcomes a roadblock presented by large genes, may be useful in other treatments, according to researchers.
